Amicus

Amicus Therapeutics Inc is a biotechnology company dedicated to discovering, developing, and providing medical treatments for individuals with rare metabolic diseases. Its main focus is on developing a pipeline of medicines for rare metabolic conditions, including a variety of rare disease gene therapy options. Its product portfolio comprises oral precision medicine for individuals with Fabry disease who have amenable genetic variants, clinical-stage treatment paradigm for Pompe disease, and a rare disease gene therapy portfolio.